🧠 Ask this record

Get an AI answer drawn only from the NIH Pandemic-Era Grants documents indexed here — every claim cited back to the filing or proceeding it came from. It will tell you plainly when the record doesn't cover your question, rather than guessing.

9873 documents

Highly Specific ZFN-Based HSC Gene Editing Therapies Identified By In Vivo Barcode Nanoparticle Screens And Rationally Designed Mrna

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

James Dahlman · GEORGIA INSTITUTE OF TECHNOLOGY · 2019 · $710,671 — Summary. Hemoglobinopathies such as β-thalassemia and sickle cell disease are genetic disorders caused by mutations in the HBB gene that codes for the β-globin component of hemoglobin. Currently, the only gene therapy available for these prevalent hereditary diseases is based on transplantation of g…

CRISPR/Cas9 somatic mutagenesis in adipose tissue

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Steven Michael Romanelli · UNIVERSITY OF MICHIGAN AT ANN ARBOR · 2019 · $37,153 — PROJECT SUMMARY The prevalence of obesity has reached pandemic levels with nearly 2 billion people worldwide considered overweight and one-third of that obese. Obesity is associated with an increased risk for type II diabetes, heart disease, and certain types of cancer which severely debilitates qua…

"NextGen Long-acting Platform: Targeted Combination Antiretrovirals"

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Ann Cornwall Collier · UNIVERSITY OF WASHINGTON · 2019 · $794,929 — The Targeted Long-acting Combination Antiretroviral Therapy (TLC-ART) Program has discovered a novel platform that can stabilize insoluble and soluble antiretroviral drugs together in a nanosuspension which provides long-acting (LA) plasma and cell concentrations in pre-clinical studies. The lead fo…

Design and characterization of biomimetic nanobiomaterials to elicit CD1-restricted T cell responses during sub-unit vaccination

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Evan Alexander Scott · NORTHWESTERN UNIVERSITY · 2019 · $685,339 — PROJECT SUMMARY Subunit vaccines combine immunodominant protein or peptide antigens from pathogens with select adjuvants, aiming to provide a more scalable, reproducible, low cost and rapid alternative to attenuated vaccines that contain live pathogens. Unfortunately, current subunit vaccines lack …

Continuous Probing of Nanoconstruct-Cell Interactions at Biologically Relevant Time Scales

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Teri Wang Odom · NORTHWESTERN UNIVERSITY · 2019 · $267,708 — PROJECT SUMMARY This proposal aims to develop live-cell, multi-channel imaging tools that can visualize—continuously, and in real time—nanoparticle interactions with cellular components. We will focus on several different time windows, where early time periods will monitor nanoparticle-cell membran…

Research Project 3: siRNA Therapy and Small Molecule Combination Treatment for Filoviruses

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Thomas William Geisbert · UNIVERSITY OF TEXAS MED BR GALVESTON · 2019 · $692,621 — PROJECT SUMMARY - Research Project 3 Members of the filovirus genera Ebolavirus and Marburgvirus are HHS Tier 1 Category A priority pathogens that cause severe and often fatal hemorrhagic fever (HF) in humans and nonhuman primates (NHPs). There are presently no approved therapeutics for ebolavirus o…

Molecular Imaging Using Cryo-EM

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Yifan Cheng · UNIVERSITY OF CALIFORNIA, SAN FRANCISCO · 2019 · $292,895 — As a versatile structure determination technology, cryo-EM is an integrated part of the HARC Center. In the past funding cycle, the Cryo-EM Core has engaged in technology development of single-particle cryo-EM, and has made major contributions to the recent technological breakthroughs in single part…

Engineering a Small Intestinal Microbiome to Evaluate Food Additive Exposure

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Gretchen Mahler · STATE UNIVERSITY OF NY,BINGHAMTON · 2019 · $303,993 — PROJECT SUMMARY Nanomaterials are increasingly used in consumer products, processed food, and food packaging, and few studies have determined the consequences of nanoparticle ingestion. The ultimate goal of this work is to determine if and how ingested metal oxide nanoparticles alter microorganism p…

Inhibition of Amyloid Formation by Heterogeneous Nanoparticles with Chaperone-like Activity

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Joel Kaar · UNIVERSITY OF COLORADO · 2019 · $198,980 — SUMMARY The formation of amyloid fibrils due to protein aggregation represents a central step in the pathogenesis of many age-related diseases for which there are no current cures. At the core of this step is the misfolding of one or more key proteins, which is converted from a natively folded or un…

New computational, transcriptional, and genome editing approaches to the biology of inflammatory bowel disease

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

GREGORY C GIBSON · GEORGIA INSTITUTE OF TECHNOLOGY · 2019 · $175,023 — Project Summary Over the past decade, the NIDDK IBDGC (Inflammatory Bowel Disease Genetics Consortium) has generated extraordinary datasets in support of genetic analysis of the onset, progression, and therapeutic response to Crohn's disease and ulcerative colitis. This Ancillary project will comple…

Cell Penetration Profiling for Biotherapeutics

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Joshua A Kritzer · TUFTS UNIVERSITY MEDFORD · 2019 · $87,299 — Cell Penetration Profiling for Biotherapeutics Biotechnology promises the ability to control biology and disease with laser-like precision. Hundreds of peptides, proteins and nucleic acids are being developed as diagnostics and therapies, but nearly all of these have poor cell penetration and unpred…

Prevention of arthritis-induced bone erosion by inhibiting osteoclast differentiation by the haloanilide, N-Methyl Dichloropropionaniline

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

John B Barnett · EXESALIBERO, INC. · 2019 · $102,161 — We are working on a new approach to treating acute arthritis based on a common pathway in the cellular infiltrates that damage bones and joints. Inflammatory arthritis disables thousands of people each year. It occurs in children and adults, after trauma and infections but most cases are idiopathic.…

Cas9 RNP delivery to immune cells in vivo via molecular targeting

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

JENNIFER A DOUDNA · UNIVERSITY OF CALIFORNIA BERKELEY · 2019 · $800,300 — PROJECT SUMMARY / ABSTRACT CRISPR-Cas9 has demonstrated incredible potential to provide clinical benefit, but the challenge of delivery currently hinders therapeutic use of genome editing in vivo. Use of viral vectors and lipid nanoparticles has established the viability of in vivo genome editing, b…

Microbubble Dose Optimization for Image-Guided Drug Delivery

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Mark Andrew Borden · UNIVERSITY OF COLORADO · 2019 · $352,275 — The development of new pharmaceuticals for the treatment of brain cancer and neurological disease has outpaced our ability to deliver them safely, largely due to the blood-brain barrier (BBB). Bypassing the BBB to access the brain parenchyma is often highly invasive, involving surgery to remove part…

The alternative complement pathway and hemocompatibility of nanosurfaces

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Dmitri Simberg · UNIVERSITY OF COLORADO DENVER · 2019 · $343,881 —  DESCRIPTION (provided by applicant): While having tremendous potential as a therapeutic tool, clinical use of engineered nanoparticles has also been associated with serious safety concerns. Following systemic injection, nanoparticles interact with blood proteins causing life-threating hypersens…

Macrophage-derived microcalcificaitons

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Elena Aikawa · BRIGHAM AND WOMEN'S HOSPITAL · 2019 · $664,893 — Project Summary This research project will test the hypothesis that, in the diabetic milieu, S100A9 induces the calcification potential of macrophage-derived extracellular vesicles (EV), precursors of microcalcifications, contributing to the biomechanical instability of the vulnerable atheroscleroti…

FIRST-IN-HUMAN TRIAL OF A RECEPTOR-TARGETED NANOPARTICLE PET TRACER FOR ATHEROSCLEROSIS

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Pamela K Woodard · WASHINGTON UNIVERSITY · 2019 · $624,055 — PROJECT SUMMARY This proposal is a first-in-human trial of a newly developed nanoparticle PET radiotracer that targets the natriuretic peptide receptor C (NPR-C), with the long-term potential to help to determine which asymptomatic patients with carotid artery stenosis might require surgery. Our res…

Acoustic-transfection using high frequency ultrasound for intracellular delivery of macromolecules into targeted single cells

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Sangpil Yoon · UNIVERSITY OF NOTRE DAME · 2019 · $248,999 — Project Summary / Abstract Dr. Sangpil Yoon is a postdoctoral scholar at the Department of Biomedical Engineering at the University of Southern California (USC). He has developed an innovative technique for the intracellular delivery of macromolecules using high frequency ultrasound. Dr. Yoon is a p…

A DNA nanotechnology vaccine platform for delivery and translation of HIV-1 1086C gp160 Env LNP

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

David Lawrence Danley · PARABON NANOLABS, INC. · 2019 · $225,220 — PROJECT SUMMARY/ABSTRACT The human immune response to HIV-1 is complex with the virus demonstrating remarkable evasion mechanisms. Significant progress has recently been made in HIV vaccine development based on early-stage clinical trials and subsequent investigations into the nature of protective i…

Lung cancer prevention and treatment by targeting ALDH1 and CD44 expressing putative lung cancer stem cells

NIH Pandemic-Era Grants · Pandemic Era Grants / 2019

Fekadu Kassie · UNIVERSITY OF MINNESOTA · 2019 · $352,275 — PROJECT SUMMARY Lung cancer is the leading cause of cancer-related death in the United States. About 90% of lung cancer cases are associated with genetic/epigenetic changes induced by tobacco smoke (TS). Although all types of lung cells could be affected by TS, the effect on stem cells is particular…