28D BLA 125742 0 07 20 2021 Memo Review

Pfizer Documents (PHMPT/FDA)

Pfizer Bla Submission

Pfizer 16 Plus Documents

10

Document text

Data Fitness Findings Report  
IND27034 
BioNTech SE and Pfizer , November  2020 
Findings  Notes  
BNT162 -01 
Title: A Multi- site, Phase I/II, 2 -Part, Dose -Escalation Trial Investigating the Safety and Immunogenicity of Four Prophylactic SARS -CoV-2 
RNA Vaccines Against COVID -19 Using Different Dosing Regimens in Healthy Adults  
 
Document / Standard  Version  Notes  
annotated CRF   Seems fine  
SDTM Implementation 
Guide  SDTM -IG v3. 2  
SDTM Controlled 
Terminology  2020-03-27  
SDTM define.xml  V2.0 Seems fine  
Medications Dictionary  WHODRUG GLOBAL 
B3 March 1, 2020   
Medical Events 
Dictionary  
(MedDRA)  V23.0  
SDTM Reviewer ’s Guide  PhUSE template  Seems fine  
 
From cSDRG : Data cutoff date of 13Aug2020 is applied by comparing XXDTC or XXSTDC from respective SDTM domains. Apart from data 
cutoff this esub is limited to cohorts described in the section 2.3.1  of cSDRG.  
  
 
 
  
FDA-CBER-2021-5683-1060075
C4591001 -ia-efficacy ( Phase 2/3 Interim Analysis ) 
Title: A Phase 1/2/3 Study to Evaluate the Safety, Tolerability, Immunogenicity, and Efficacy of RNA Vaccine Candidates Against COVID -
19 in Healthy Individuals.  
 
Document / Standard  Version  Notes  
annotated CRF   Seems fine  
SDTM Implementation 
Guide  SDTM -IG v3.2   
SDTM Controlled 
Terminology  2020-03-27  
SDTM define.xml  V2.0  Seems fine  
Medications Dictionary  WHODD 
GLOBALV3Mar20, 
WHO DDE v202003   
Medical Events 
Dictionary  
(MedDRA)  V23.1  
SDTM Reviewer’s Guide  PhUSE template  Seems fine  
 
From cSDRG: The IA efficacy analysis data with a cutoff of 4NOV2020 was included in this submission. In addition, a subject cutoff  to 
exclude phase 1 subjects was also applied to the data. Only subjects in Phase 2/3 that had informed consent date after 27JUL2 020 were 
included.  
 ADaM folder contains: adc19ef, adsl, adsympt  
 
 
    
 
  
 
FDA-CBER-2021-5683-1060076
C4591001 -safety -fa-eff (Final Efficacy/EUA Safety Analysis ) 
Title: A Phase 1/2/3 Study to Evaluate the Safety, Tolerability, Immunogenicity, and Efficacy of RNA Vaccine Candidates Against COVID -
19 in Healthy Individuals.  
 
Document / Standard  Version  Notes  
annotated CRF   Seems fine  
SDTM Implementation 
Guide  SDTM -IG v3.2   
SDTM Controlled 
Terminology  2016 -12-16  
SDTM define.xml  V2.0  Seems fine  
Medications Dictionary  GLOBALB3Mar19   
Medical Events 
Dictionary  
(MedDRA)  V21.1   
SDTM Reviewer’s Guide  PhUSE template  Seems fine  
 
From cSDRG: The final analysis data with a cutoff of 14NOV2020 was included in this submission. Screen failure data was also dropped 
as part of the cutoff process. Details about the cutoff algorithm applied to the SDTM data :  
All records with ASTDT <= &cutoff are included. In addition,  
If .<ASTDT <= &cutoff and AEENDT > cutoff date, then - AEENDTC and AEENDY is set to missing  
- AEENRTPT = ‘ONGOING’  
- AEENTPT = ‘Last Subject Encounter’  
- AEOUT = ‘NOT RECOVERED/NOT RESOLVED’  
end;  
else if AESTDTC = ‘ ‘ and AEENDTC ne ‘ ‘and AENDT <=  
&cutoff then the record is included.  
If AESTDTC and AEENDTC are both missing  then the record 
is included.  
DROP ASTDT and AENDT  
 
ADaM folder contains: adae, adc19ef, adcevd, adds, adfacevd, admh, adsl, adsympt, adva  
 
FDA-CBER-2021-5683-1060077
Data Issues  
  
Missing MedDRA coding data  
• Study c4591001- ia-efficacy:  
aedecod  aeptcd  aellt  aelltcd  aehlt  aehltcd  aehlgt  aehlgtcd  aebodsys  aebdsycd  aesoc  aesoccd  Freq  
populated  null null null null null null null null null null null 97 
populated  populate
d populate
d populate
d populate
d populated  populated  populated  populated  populated  populated  populated  16670  
 
• Study c4591001- safety -fa-eff 
aedecod  aeptcd  aellt  aelltcd  aehlt  aehltcd  aehlgt  aehlgtcd  aebodsys  aebdsycd  aesoc  aesoccd  Freq  
populated  null null null null null null null null null null null 89 
populated  populate
d populate
d populate
d populate
d populate
d populated  populated  populated  populated  populated  populated  20228  
 
• Note: For both studies, AEDECOD = ‘Uncoded’ when the rest of the MedDRA levels are null . In ADAE (for study c4591001- safety -
fa-eff), for these uncoded records, AEDECOD values are a copy of AETERM, but upper cased, and two @ symbols attached. For 
example, AETERM ‘Injection site pain’ has ADAE.AEDECOD = ‘INJECTION SITE PAIN@@’  
• cSDRG  explanation: Study was ongoing at the time of data cutoff therefore some AE terms were not yet coded in MedDRA. 
These terms were set to 'Uncoded' in AE dataset for transparency. These terms will be coded for the final reporting event for  
this study once the study is completed.  
  
Subjects have multiple D ISPOSITION EVENT records for the same EPOCH and DSSTDTC  
• Studies c4591001- ia-efficacy and c4591001- safety -fa-eff 
• Need to use SUPPDS.DSPHASE to distinguish whether its VACCINATION or FOLLOW -UP or SCREENING  
• Example  of just a few out of many subjects  in c4591001- safety -fa-eff: 
usubjid  dsseq  dsterm  dsdecod  dscat  epoch  dsstdtc  dsstdy  suppds.dspha
se 
C4591001 1005 10051308  5 busy work schedule  WITHDRAWAL BY 
SUBJECT  DISPOSITION 
EVENT  VACCINATION  10/19/2020  1 FOLLOW -UP 
C4591001 1005 10051308  4 busy work schedule  WITHDRAWAL BY 
SUBJECT  DISPOSITION 
EVENT  VACCINATION  10/19/2020  1 VACCINATION  
C4591001 1005 10051308  1 COMPLETED  COMPLETED  DISPOSITION 
EVENT  VACCINATION  10/19/2020  1 SCREENING  
C4591001 1013 10131017  5 SUBJECT WITHDREW 
CONSENT FROM 
STUDY.  WITHDRAWAL BY 
SUBJECT  DISPOSITION 
EVENT  SCREENING  7/30/2020  1 FOLLOW -UP  
FDA-CBER-2021-5683-1060078
C4591001 1013 10131017  4 SUBJECT CHANGED 
HIS DECISION AND 
WAS RANDOMIZED INTO SYSTEM.  WITHDRAWAL BY 
SUBJECT  DISPOSITION 
EVENT  SCREENING  7/30/2020  1 VACCINATION  
C4591001 1013 10131017  1 COMPLETED  COMPLETED  DISPOSITION 
EVENT  SCREENING  7/30/2020  1 SCREENING  
 
 
Subjects have AE records with AEACN = DRUG WITHDRAWN but no ADVERSE EVENT record in DS  
• Study BNT162- 01 – see report “ IND27034 - BNT162- 01 - AEACN is DRUG WITHDRAWN but no ADVERSE EVENT record in DS.xlsx ” 
• Study c45 91001- ia-efficacy – see report “ IND27034 -  c4591001- ia-efficacy - AEACN is DRUG WITHDRAWN but no ADVERSE 
EVENT reco rd in DS.xlsx ” 
• Study c4591001- safety -fa-eff – see report “ IND27034 -  c4591001- safety -fa-eff - AEACN is DRUG WITHD RAWN but no ADVERSE 
EVENT record in DS.xlsx ” 
  
Subjects have multiple baseline records in VS  
• Study BNT162 -01 – 40 records, 5 subjects  – see report “ IND27034 - BNT1 62-01 - Multiple baseline records in VS.xlsx ” 
 
Subjects have multiple baseline records in LB  
• Study BNT162 -01 – 100 records, 5 subjects – see report “ IND27034 - BNT162- 01 - Multiple baseline records in LB.xlsx ” 
  
Reactogenicity events in CE with a duration of at least 7 days, but aren’t in the AE domain  
• Study BNT162- 01 – 13 records  
usubjid  ceterm  cestdtc  ceendtc  
BNT162 -01-276-01-0003  Injection site reaction - Tenderness  5/19/2020  5/26/2020  
BNT162 -01-276-01-0005  Fatigue  5/15/2020  5/22/2020  
BNT162 -01-276-01-0010  Fatigue  4/24/2020  5/2/2020  
BNT162 -01-276-01-0010  Headache  4/25/2020  5/2/2020  
BNT162 -01-276-01-0010  Injection site reaction - Pain  4/25/2020  5/2/2020  
BNT162 -01-276-01-0010  Injection site reaction - Tenderness  4/25/2020  5/2/2020  
BNT162 -01-276-01-0010  Malaise  4/25/2020  5/2/2020  
BNT162 -01-276-01-0010  Myalgia  4/25/2020  5/2/2020  
BNT162 -01-276-01-0019  Headache  5/20/2020  5/27/2020   
FDA-CBER-2021-5683-1060079
BNT162 -01-276-02-0156  Injection site reaction - Tenderness  7/23/2020  7/30/2020  
BNT162 -01-276-02-0160  Fatigue  6/29/2020  7/7/2020  
BNT162 -01-276-02-0160  Headache  6/30/2020  7/7/2020  
BNT162 -01-276-02-0160  Malaise  6/30/2020  7/7/2020  
 
 
DDDTC date is after RFPENDTC  
• Study c4591001- ia-efficacy - 1 records (33.33%)  
USUBJID  DDTEST  DDORRES  DDDTC  RFPENDTC  Last Disposition 
date  DSDECOD  
C4591001 1162 11621327  PRIMARY CAUSE OF 
DEATH  atherosclerotic 
disease  9/24/2020  9/13/2020  9/13/2020  DEATH  
 
• Study c4591001- safety -fa-eff - 3 records (50%)  
USUBJID  DDTEST  DDORRES  DDDTC  RFPENDTC  Last Disposition 
date  DSDECOD  
C4591001 1066 10661350  PRIMARY CAUSE OF 
DEATH  myocardial infarction  11/10/2020  11/3/2020  11/3/2020  DEATH  
C4591001 1081 10811194  PRIMARY CAUSE OF 
DEATH  Cause is currently 
unknown. Detail will 
be updated once the death certificate has 
been received  11/11/2020  11/1/2020  11/1/2020  DEATH  
C4591001 1162 11621327  PRIMARY CAUSE OF 
DEATH  atherosclerotic 
disease  9/24/2020  9/13/2020  9/13/2020  DEATH  
 
EXSTDTC /EXENDTC  date is after RFPENDTC  
• Study c4591001- ia-efficacy - 25 records (0.03%)  
USUBJID  EXTRT  EXSTDTC  RFPENDTC  
C4591001 1013 10131358  Placebo  2020 -10-06T14:32:00  9/21/2020  
C4591001 1013 10131622  BNT162b2  2020 -10-28T15:20:00  10/19/2020  
C4591001 1019 10191178  BNT162b2  2020 -10-08T12:09:00  9/30/2020  
C4591001 1024 10241117  Placebo  2020 -10-16T16:10:00  10/7/2020   
FDA-CBER-2021-5683-1060080
C4591001 1028 10281292  Placebo  2020 -10-30T09:15:00  10/29/2020  
C4591001 1044 10441116  Placebo  2020 -10-29T10:11:00  10/5/2020  
C4591001 1044 10441165  BNT162b2  2020 -10-19T10:40:00  10/6/2020  
C4591001 1044 10441214  BNT162b2  2020 -10-30T10:18:00  10/22/2020  
C4591001 1072 10721037  Placebo  2020 -10-07T12:34:00  9/9/2020  
C4591001 1084 10841481  Placebo  2020 -11-02T11:25:00  10/29/2020  
C4591001 1088 10881045  BNT162b2  2020 -10-26T10:53:00  9/8/2020  
C4591001 1088 10881080  Placebo  2020 -10-12T16:44:00  9/11/2020  
C4591001 1088 10881139  BNT162b2  2020 -10-15T14:05:00  9/21/2020  
C4591001 1092 10921175  Placebo  2020 -11-04T09:30:00  9/9/2020  
C4591001 1097 10971118  Placebo  2020 -10-15T09:49:00  10/13/2020  
C4591001 1098 10981209  Placebo  2020 -10-15T14:36:00  10/13/2020  
C4591001 1107 11071189  Placebo  2020 -10-07T13:04:00  9/22/2020  
C4591001 1109 11091408  BNT162b2  2020 -10-07T15:49:00  9/22/2020  
C4591001 1128 11281353  Placebo  2020 -10-19T10:00:00  10/5/2020  
C4591001 1141 11411096  BNT162b2  2020 -10-13T13:23:00  9/24/2020  
C4591001 1156 11561193  BNT162b2  2020 -10-21T15:14:00  10/20/2020  
C4591001 1226 12261684  BNT162b2  2020 -10-16T13:05:00  10/2/2020  
C4591001 1226 12261821  Placebo  2020 -10-22T08:53:00  10/8/2020  
C4591001 1226 12262353  Placebo  2020 -10-23T11:25:00  10/20/2020  
C4591001 1247 12471092  Placebo  2020 -10-29T12:07:00  10/20/2020  
 
• Study c4591001- safety -fa-eff - 18 records (0.02%)  
USUBJID  EXTRT  EXSTDTC  RFPENDTC  
C4591001 1013 10131544  BNT162b2  2020 -11-04T13:47:00  10/5/2020  
C4591001 1013 10131622  BNT162b2  2020 -10-28T15:20:00  10/19/2020  
C4591001 1013 10131738  BNT162b2  2020 -11-11T15:27:00  11/5/2020  
C4591001 1024 10241117  Placebo  2020 -10-16T16:10:00  10/7/2020  
C4591001 1028 10281292  Placebo  2020 -10-30T09:15:00  10/29/2020  
C4591001 1044 10441116  Placebo  2020 -10-29T10:11:00  10/5/2020  
FDA-CBER-2021-5683-1060081
C4591001 1044 10441214  BNT162b2  2020 -10-30T10:18:00  10/22/2020  
C4591001 1056 10561232  Placebo  2020 -11-04T12:40:00  10/7/2020  
C4591001 1079 10791143  Placebo  2020 -11-06T15:33:00  9/9/2020  
C4591001 1079 10791264  BNT162b2  2020 -11-04T13:48:00  9/30/2020  
C4591001 1088 10881045  BNT162b2  2020 -10-26T10:53:00  9/8/2020  
C4591001 1120 11201299  BNT162b2  2020 -10-19T13:48:00  10/12/2020  
C4591001 1122 11221052  Placebo  2020 -11-13T13:15:00  10/30/2020  
C4591001 1123 11231345  Placebo  2020 -11-05T09:46:00  11/2/2020  
C4591001 1156 11561193  BNT162b2  2020 -10-21T15:14:00  10/20/2020  
C4591001 1226 12261797  BNT162b2  2020 -11-06T12:36:00  10/7/2020  
C4591001 1226 12262083  Placebo  2020 -11-07T09:18:00  10/27/2020  
C4591001 1247 12471092  Placebo  2020 -10-29T12:07:00  10/20/2020  
 
 
cSDRG  explanation: “At the time of data extraction, study is still ongoing and RFPENDTC is derived as the maximum of date of  
disposition, Subject Visits, date of death. Therefore for ongoing subjects may not yet include completion date of the current  study pha se  
where individual dates from that phase may already be reported.”  
 
DSSTDTC is before RFICDTC  
• Study c4591001- ia-efficacy - 4 records (0%)  
USUBJID  DSDECOD  DSSTDTC  SUB:RFICDTC  SUPPDS.DSPHASE  
C4591001 1161 11611011  COMPLETED  8/1/2020  8/19/2020  SCREENING  
C4591001 1161 11611011  RANDOMIZED  8/1/2020  8/19/2020   
C4591001 1213 12131020  RANDOMIZED  11/2/2020  11/3/2020   
C4591001 1213 12131021  RANDOMIZED  11/2/2020  11/3/2020   
 
• Study c4591001- safety -fa-eff - 3 records (0%)  
USUBJID  DSDECOD  DSSTDTC  SUB:RFICDTC  SUPPDS.DSPHASE  
C4591001 1097 10971003  PROTOCOL 
DEVIATION  8/17/2020  8/19/2020  FOLLOW -UP 
C4591001 1161 11611011  COMPLETED  8/1/2020  8/19/2020  SCREENING   
FDA-CBER-2021-5683-1060082
C4591001 1161 11611011  RANDOMIZED  8/1/2020  8/19/2020   
 
cSDRG  explanation: “At the time of data extraction study is still ongoing and data cleaning is still occurring. Updated data will be   
included for future reporting events and at study completion.”  
 
Value for LBSTNRHI is less than value for LBSTNRLO  
• Study c4591001- ia-efficacy - 1 records (0.06%)  
o cSDRG explanation: “Subject C4591001 1047 10471252 has one record where LBTESTID=BILI with LBSTHRHI=1.7 and  LBSTNRLO=17.1. Data is reported as collected. At the time of data extraction study is still ongoing and data cleaning is  
still occurring. Updated data will be included for future reporting events and at study completion.”  
• Study c4591001- safety -fa-eff - 12 records (0.06%)  
o cSDRG explanation: “Data is reported as collected. At the time of data extraction s tudy is still ongoing and data cleaning  
is still occurring. Updated data will be included for future reporting events and at study completion.”  
 
study  usubjid  lbtestcd  lbstresu  lbstnrlo  lbstnrhi  lbspec  
C4591001 -ia-efficacy  C4591001 1047 10471252 BILI umol/L  17.1  1.7 BLOOD  
C4591001 -safety -fa-eff C4591001 1082 10821143  LYM  10^9/L  1.5 0.7 BLOOD  
C4591001 -safety -fa-eff C4591001 1110 11101357  CD4 10^9/L  0.49  0.174  BLOOD  
C4591001 -safety -fa-eff C4591001 1194 11941073  CD4 10^9/L  0.453  0.157  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041152  CD4 10^9/L  0.3 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041154  CD4 10^9/L  0.3 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041162  CD4 10^9/L  0.2 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041164  CD4 10^9/L  0.3 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041165  CD4 10^9/L  0.393  0.149  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041176  CD4 10^9/L  0.3 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041216  CD4 10^9/L  0.3 0.17  BLOOD  
C4591001 -safety -fa-eff C4591001 1204 12041233  CD4 10^9/L  0.49  0.174  BLOOD  
C4591001 -safety -fa-eff C4591001 1246 12461073  CD4 10^9/L  0.358  0.126  BLOOD  
 
  
MHSTDTC date is after RFSTDTC  (which typically means it should be an AE, not MH)  
• Study c4591001- ia-efficacy - 2 records (0%)  
• Study c4591001- safety -fa-eff - 3 records (0%)  
  
FDA-CBER-2021-5683-1060083
cSDRG explanation: “At the time of data extraction study is still ongoing and data cleaning is still occur ring. Updated data will be  
included for future reporting events and at study completion.”  
 
STUDYID  USUBJID  MHTERM  MHDECOD  MHSTDTC  RFSTDTC  
C4591001 -ia-efficacy  C4591001 1110 11101299  prostatectomy  Prostatectomy  10/1/2020  2020 -09-
24T11:27:00  
C4591001 -ia-efficacy  C4591001 4444 44441233  Ahmed valve tube 
shortening  Glaucoma surgery  9/23/2020  2020 -09-
21T20:30:00  
C4591001 -safety -fa-eff C4591001 1007 10071418  Bone spur removal  Bone lesion excision  11/5/2020  2020 -10-
22T14:15:00  
C4591001 -safety -fa-eff C4591001 1095 10951180  Atrial Septal Defect  Atrial septal defect  11/5/2020  2020 -08-
31T12:08:00  
C4591001 -safety -fa-eff C4591001 1133 11331285  RIGHT HAND 
TENOLYSIS  Tenolysis  9/11/2020  2020 -08-
27T13:30:00  
 
 
 
FDA-CBER-2021-5683-1060084