28L BLA 125742 0 07 20 2021 Memo Review

Pfizer Documents (PHMPT/FDA)

Pfizer Bla Submission

Pfizer 16 Plus Documents

2

Document text

Data Fitness Findings Report  
IND27034 
BioNTech SE and Pfizer , April  2021 
Findings  Notes  
C4591001  EUA Amendment (12 -15 Years of Age)  
Title: A Phase 1/2/3 Study to Evaluate the Safety, Tolerability, Immunogenicity, and Efficacy of RNA Vaccine Candidates Against COVID -
19 in Healthy Individuals.  
 
Document / Standard  Version  Notes  
annotated CRF   Seems fine  
SDTM Implementation 
Guide  SDTM -IG v3.2   
SDTM Controlled 
Terminology  2020-03-27  
SDTM define.xml  V2.0  Seems fine  
Medications Dictionary  WHODD 
GLOBALV3Mar20, 
WHO DDE v202003   
Medical Events 
Dictionary  
(MedDRA)  V23.1  
SDTM Reviewer’s Guide  PhUSE template  Seems fine  
 
 
 
   
  
FDA-CBER-2021-5683-1066331
Data Issues  
  
Adverse event marked as AEREL = RELATED, but subject didn’t receive dose yet  
• USUBJID = C4591001 1226 12261520, AETERM = Pain at injection site , AESTDTC = 2020- 09-02T21:00 
o 2 EX records: EXSTDTC = 2020- 09-03T15:06:00 and 2020- 09-22T10:22:00 
  
Subjects have AE records with AEACN = DRUG WITHDRAWN but no ADVERSE EVENT record in DS  
• 20 subjects – see report “ IND27034 - 12-15years - AEACN of DRUG WITHDRAWN but no DS ADVERSE EVENT record.xlsx ” 
  
Value for CEHLGT n ot found in MedDRA dictionary  
• 1 record (0%)  
• cSDRG explanation: “Manually coded as "Virus infectious disorders". ” 
• The correct value per the MedDRA dictionary is: Viral infectious disorders  
  
Inconsistent coding of MHTERM  
mhterm  mhdecod  mhhlt  mhhlgt  mhbodsys  STUDYID  count_of
_mhs  meddrav  
SKIN CANCER  SKIN CANCER  SKIN NEOPLASMS 
MALIGNANT AND 
UNSPECIFIED (EXCL 
MELANOMA)  SKIN NEOPLASMS 
MALIGNANT AND UNSPECIFIED  NEOPLASMS BENIGN, 
MALIGNANT AND UNSPECIFIED (INCL 
CYSTS AND POLYPS)  C4591001  2 23.1  
SKIN CANCER  SKIN NEOPLASM 
EXCISION  SKIN LESION 
EXCISIONS  SKIN AND 
SUBCUTANEOUS 
TISSUE THERAPEUTIC 
PROCEDURES  SURGICAL AND MEDICAL 
PROCEDURES  C4591001  1 23.1  
 
  
 
FDA-CBER-2021-5683-1066332