Pneumococcal 05 Kobayashi 508

CDC ACIP — Vaccine Advisory Committee

Acip

Slides

57

Document text

Nationa  l Center  for  Immunizatio  n &  Respirator  y Diseases 
     
        
   
   
    
  Evidence to Recommendations Framework (Preliminary): 
Use of 20-valent Pneumococcal Conjugate Vaccine in U.S. Children 
Miwako Kobayashi, MD, MPH 
Pneumococcal Vaccines Work Group 
Advisory Committee on Immunization Practices 
February 22, 2023 
    
        
        
      
       
           
           
   
         
      
     
          
          Evidence to Recommendations (EtR) framework 
EtR Domain Question 
Public Health Problem • Is the problem of public health importance? 
Benefits and Harms • How substantial are the desirable anticipated effects? 
• How substantial are the undesirable anticipated effects? 
• Do the desirable effects outweigh the undesirable effects? 
• What is the overall certainty of this evidence for the critical outcomes? 
Values • Does the target population feel the desirable effects are large relative 
to the undesirable effects? 
• Is there important variability in how patients value the outcomes? 
Acceptability • Is the intervention acceptable to key stakeholders? 
Feasibility • Is the intervention feasible to implement? 
Resource Use • Is the intervention a reasonable and efficient allocation of resources? 
Equity • What would be the impact of the intervention on health equity?2 
    
        
        
      
       
           
           
   
         
      
     
          
          Values •Does the target population feel the desirable effects are large relative
to the undesirable effects?
•Is there important variability in how patients value the outcomes?
Acceptability •Is the intervention acceptable to key stakeholders?
Feasibility •Is the intervention feasible to implement?
Resource Use •Is the intervention a reasonable and efficient allocation of resources?Evidence to Recommendations (EtR) framework 
EtR Domain Question 
Public Health Problem • Is the problem of public health importance? 
Benefits and Harms • How substantial are the desirable anticipated effects? 
• How substantial are the undesirable anticipated effects? 
• Do the desirable effects outweigh the undesirable effects? 
• What is the overall certainty of this evidence for the critical outcomes? 
Equity • What would be the impact of the intervention on health equity?3 
         
  
      
    
 
       All children under age 2 years have the same 
pneumococcal vaccine recommendations 
• 3 primary series and a booster=“3+1” schedule 
PCV PCV PCV PCV 2months 4months 12–15 months 6months 
Primary Series Booster 
Either PCV13 or PCV15 can be used for U.S. children. 
4 
        
  
      
    
 
                  
    
     
      Primary Series Booster
Currently, either PCV13 or PCV15 can be used for U.S. children.All children under age 2 years have the same 
pneumococcal vaccine recommendations 
• 3 primary series and a booster=“3+1” schedule 
PCV PCV PCV PCV 2months 4months 12–15 months 6months 
Should PCV20 be recommended as an option for 
pneumococcal conjugate vaccination according to currently recommended dosing and schedules, for U.S. children aged <2 years? 
5 
        
     
 
 
 
   
  
  
   
 
   
 Children age ≥2 years with certain underlying conditions 
recommended to receive PPSV23 in addition 
PPSV23 Recommended 
PCV doses Recommended 
PCV doses Healthy 
children 
MC, CSF leak, 
cochlear 
implant 
≥8 weeks 
Recommended 
PCV doses PPSV23 PPSV23 Immuno-
ompromised 
≥8 weeks ≥5 years 
MC aged 6–18 
years PPSV23 
                 
         
           
  C
c
C
Note: Excludes catch-up vaccination schedules. 
CMC=chronic medical conditions, including chronic heart disease, chronic lung disease, diabetes mellitus 
CSF=cerebrospinal fluid 
Use of 15-Valent Pneumococcal Conjugate Vaccine Among U.S. Children: Updated Recommendations of the Advisory Committee on Immunization 
Practices — United States, 2022 | MMWR (cdc.gov) 6 
      
       
       
       
 
Should PCV20 without PPSV23 be recommended 
as an option for pneumococcal vaccination for U.S. children aged 2–18 years with underlying 
medical conditions that increase the risk of pneumococcal disease? 
7 
           
  
           
  
    
     
         
      
  
         PICO 
Question Should PCV20 be recommended as an option for pneumococcal vaccination 
for U.S. children? 
Population U.S. children aged 2–18 years with All U.S. children aged <2 years underlying medical conditions 
Intervention PCV20 according to currently 
recommended dosing and PCV20 (without PPSV23) schedules 
Comparison PCV13 or PCV15 according to currently recommended dosing and schedules 
Outcomes VT-IPD, VT- pneumonia, VT- AOM, VT- pneumococcal deaths, serious adverse events following vaccination 
8 VT: vaccine-type, IPD: invasive pneumococcal disease, AOM: acute otitis media 
EtR Dom  ain: P  ublic Healt  h Problem 
     
 
          
    
          
          
           
     
          
    
    
     
     Summary of pneumococcal disease epidemiology 
in children 
• Use of PCVs (PCV7, PCV13) significantly decreased the incidence of 
pneumococcal disease in U.S. children. 
• Outpatient ARIs caused by pneumococcus, such as AOM, sinusitis, and pneumonia, are common causes of outpatient visits and antibiotic prescribing. 
• Risk of disease remains high in children with underlying conditions that increase the risk of pneumococcal disease. 
• In 2018–2019, the proportion of IPD caused by vaccine serotypes was: 
• PCV20, non-PCV13: ~30% of IPD 
• PCV15, non-PCV13: ~15% of IPD 
Gierke. February 2023 ACIP meeting presentation 
King. February 2023 ACIP meeting presentation 10 
  
         
 Public Health Problem 
Is pneumococcal disease of public health importance in U.S. 
children? 
□
□□□□□ N o 
 Probably  no 
 Probably  yes 
 Yes  Varies  Don’t  know 
11 
  
         
 
     
        
    
      
         
  Public Health Problem 
Is pneumococcal disease of public health importance in U.S. 
children? 
□ 
□ □ □ □ □ N o 
Probably  no 
Probably  yes 
Yes Varies Don’t  know • Variability in Work Group members’ 
interpretations for children aged <2 years due to significant reductions in pneumococcal disease. 
• Most agreed that pneumococcal disease continues to be of public health importance due to the remaining disease burden. 
12 
EtR Dom  ain: Benefits   and Harms 
 
  
  
  
     
     
    
   
  
       
 Outcomes (Benefits) 
Outcome Importance Description 
VT- IPD Critical Studies assessing PCV20 against these 
VT- non-bacteremic 
pneumococcal pneumonia clinical outcomes are currently not Critical 
available 
VT- acute otitis media  PCV20 immunogenicity studies for Critical GRADE 
VT- pneumococcal deaths Critical  PCV13/PPSV23 clinical outcome studies for background 
AOM=acute otitis media, IPD=invasive pneumococcal disease, VT=vaccine-type 14 
 
 
       Outcomes (Harms) 
Outcome Importance Description 
Serious adverse events Critical Safety data for PCV20 are available 
15 
Background 
     
  
   
 
 
 
            
             
            PCV13 effectiveness (3+1) in children, VT-IPD 
Study Population Dosin  g schedule  
(Ye  ar o  f 
introduction) Me thod Outcome Vaccine (95% CI) 
Effectiveness 
Savulescu, 
2022 Children 2m – 59m; Spidnet 
(12 European 2+1 or 3+1 
(variable) Indirect cohort 3 + 1 doses, ≥12 months 89.7% (adjusted*) (82, 94) 
sites, 2012 -
2018 
V an 
de  r 
Linden,  
2016* Childre  n <2  
years;  German  y 
(GNRCS) 3+1  (Decembe  r 
2009) Indirec  t 
cohort PCV13-type;  post-booster 91% (61,  99) 
Weinberger,  
2016 Childre  n 2.5  – 
56m;  German  y 
(ESPED) 3+1  (Decembe  r 
2009) Indirec  t 
cohort PCV13-type  +6C;  ≥2  dose  before  12  
months  or one  dose  on/afte  r 12  
months 85%  (adjusted) (64,  94) 
Dominguez,  
2017 Childre  n 7m  -
59m;  Sp  ain 
(Catalonia) 3+1  (public,  Ju ly 
2016) Matche  d 
case-
control PCV13-type;  7-59m;  ≥2  doses  before  
12 months  o r one  dose  afte  r 12  
months 78.9% (52.8,  90.5) 
Moore  , 
2016 Childre  n 2-
59m;  US 3+1  (2010) Matche  d 
case-
control PCV13-type;  ≥1  dose 86.0%  
(unadjusted) (75.5,  92.3) 
* Adjusted by site, age, year of notification and at least one underlying disease 
Post-licensure vaccine effectiveness studies have shown that PCV13 is highly effective against 
VT-IPD 17 
   
  
   
 
     
      
         
       
 PCV13 effectiveness, VT-pneumococcal pneumonia 
Study Population Dosing schedule 
(Year of introduction) Method Outcome VE (95% CI) 
Zhang, 2021 Children  born  
D
ecember  2016  
– Novembe  r 
2018,  China 3+1  (2017) Indirect  cohort; 
VT-CAP  defined  as  hospita  l 
discharge  diagnosis code  of  
pneumonia  +  deep  uppe  r 
respiratory  aspirate  with  
PCV13  serotypes.  VT-CAP;  ≥3  
doses 62.1  % 
(adjusted) (26.3  , 80.5) 
Lew
nard, 
2021* Children 4 to 59 
months, Israel 2+1 (2010) Nested  c ase-control  ; 
Used: • PCV-conferred  protection  
against VT  pneumococca  l 
carriage 
• Protection  agains  t 
progression  fr  om carriage  t o 
pneumonia CAP attributed  
t o PCV13  , 12-
59  months;  2+1  
doses 77
.0 % 
(adjusted) (-16.0, 100.0) 
CAP=community acquired pneumonia 
*funded by Pfizer Limited data on PCV13 effectiveness against VT-pneumococcal 
pneumonia in children. PCV13 likely protective. 18 
  
  
   
 
    
          
     
          
        
          
    PCV13 effectiveness, VT-AOM 
Study Population Dosing schedule 
(Year of introduction) Method Outcome VE (95% CI) 
Pichichero, 
2018* Children  ≤ 36  
month  s, United  
States 3+1  (2010) Prospective  
longitudina  l 
cohor  t (PCV1  3 v  
PCV  7 period) PCV13-non-PCV7 serotype  s; 
PCV1  3 full  primar  y serie  s 
(regardle  ss of  booste  r statu  s) 
vs. PCV7  f or middle-ear  flui  d 
samples  a t onse  t of  AOM 
Serotype  3; PCV13  ful l 
primary  serie  s (regardle  ss of  
booste  r status)  vs. PCV  7 f  or 
middle-ear  fluid  samples  a t 
onse  t of  AOM 86  % 
(adjusted) 
5 % 
(adjusted) (61 , 94) 
(–181  , 68) 
Oc
hoa-
Gondar, 2015 ≤14 years; Spain 
(Catalonia region) 3+1 (2016, publicly available) Indirect cohort PCV13-type; ≥1 dose 62% (unadjusted) (-141, 95) 
Dagan, 2021* Children 5 to 35 months, Israel 2+1 (2010) Nested case-control PCV13-type; ≥2 doses vs. 0 doses 77.4% (adjusted) (35.3, 92.1) 
Serotype 3; ≥2 doses vs. 0 doses 89.0% (adjusted) (23.9, 98.4) 
Limited data on PCV13 effectiveness against VT-pneumococcal AOM in 
children. PCV13 likely protective. *funded by Pfizer 19 
     
          
     PPSV23 effectiveness, VT-IPD (Pre-PCV U.S. data) 
Pre-PCV era data showed that PPSV23 is protective against VT-IPD among 
children with underlying medical conditions. 
    Fiore et al. EID 1999 20 
    
            
       
 
     
     
    
      PPSV23 effectiveness, non-invasive pneumococcal 
disease 
• No study on PPSV23 VE against AOM identified in a recent systematic review1 
• Two randomized-controlled trials (RCTs)2,3 evaluated PCV7-PPSV23 in series 
against AOM 
• No efficacy in the PCV7-PPSV23 groups 
1. Marra et al. Value Health 2022 
2. Veenhoven et al. Lancet 2003 
3. Van Kempen et al. Int J Pediatr Otorhinolaryngol 2006 21 
GRADE:  PCV2  0 us  e  in children 
     
       Evidence retrieval: PCV20 use in children 
Clinicaltrials.gov 
N=12 
4 studie  s include  d fo  r GRADE 
Phase  I I tria  l (published),  N=1 
Phase  II I trial  s (unpublished),  N=3 Pubmed 
N=62 
PCV20  routi  ne use 
(N=3) 
Immunogenicity  (N=2) 
Safety  (N=3) PCV20   use i  n childre  n 
wit  h underlyi  ng 
conditions 
(N=1) 
Immunogenicity  (N=1) 
Safety  (N=1) Unpublishe  d data  from  
pharmaceutica  l 
company 
N=3 
23 Search terms used are provided in supplementary slides 
   
    
         
       
    
  
           
  
   
           
   
         
       
     
              
    
    Summary of evidence: 
Benefits, children <2 years 
• Informed by 2 randomized controlled trials (Phase II and III)1,2 
• Healthy children randomized to either PCV13 or PCV20 
• PCVs given using 3+1 schedule 
• Summary of findings 
•PCV20 had numerically lower immune responses* vs. PCV13 for most of the 
13 shared serotypes 
•Post dose 3 : 
•PCV20 did not meet noninferiority criteria vs. PCV13 for some serotypes 
•Post dose 4 : 
•PCV20 noninferior to PCV13 for all 13 shared serotypes 
•PCV20 noninferior to PCV13** for all 7 additional serotypes 
*measured as IgG GMCs and GMRs 
**Compared with the serotype with lowest immune response among PCV13 serotypes except for serotype 3 
1. Senders et al. PIDJ 2021 
2. Pfizer unpublished data from B7471011 24 
   
    
             
 
      
     
    
   
          Summary of evidence: 
Harms, children <2 years 
• Serious adverse events (SAEs) across 3 studies (dose 1 through 6 months after 
dose 4): 
• PCV20: 4.5% (n=1,567) vs PCV13: 3.7% (n=1,376) 
• None were considered to be vaccine-related 
1. Senders et al. PIDJ 2021 
2. Pfizer B7471011, unpublished data 
3. Pfizer B7471013, unpublished data, limited to US and Puerto Rico sites 25 
          
          
   
  
   
 
 
  
         Should PCV20 be recommended as an option for pneumococcal conjugate 
vaccination according to currently recommended dosing and schedules, for U.S. children aged <2 years? 
Type Outcome Importance Included in 
evidence profile Certainty for 
healthy individuals 
VT- IPD Critical Yes Moderate 
Benefits VT-pneumonia Critical Yes Moderate 
VT- AOM Critical Yes Moderate 
VT- pneumococcal 
deaths Critical Yes Moderate 
Harms SAEs following 
vaccination Critical Yes Moderate 
AOM=acute otitis media, IPD=invasive pneumococcal disease, SAE=serious adverse events, VT=vaccine-type 26 
  
     
       
    
   
 
    
   
     
   Benefits and Harms 
How substantial are the desirable anticipated effects? 
 Routine PCV20 use for children aged <2 years 
□ Minimal 
 Small 
 Moderate  Large  Varies  Don’t  know □□□□□• PCV20 provides the broadest 
serotype coverage among available PCVs. 
• Unknown how substantial the protection conferred from PCV20 will be based on available data. 
27 
  
     
        Benefits and Harms 
How substantial are the undesirable anticipated effects? 
 Routine PCV20 use for children aged <2 years 
□ Minimal 
Small 
Moderate Large Varies Don’t  know □ □ □ □ □ 
28 
  
       
       
  
  
   Benefits and Harms 
Do the desirable effects outweigh the undesirable effects? 
 Routine PCV20 use for children aged <2 years 
□ Favor  s intervention* 
 Favor  s current  recommendation
 Favor  s both 
 Favor  s neither 
 Varies 
 Don’t  know □  
□□□□
*Intervention: PCV20 use 
Comparison: PCV13 or PCV15 use 29 
  
       
       
  
           
 
    
         
         
      Benefits and Harms 
Do the desirable effects outweigh the undesirable effects? 
• Routine PCV20 use for children aged <2 years 
Favors Intervention (PCV20): 
• PCV20 is expected to prevent more disease compared with current PCVs (PCV13, PCV15) 
Favors Both (PCV20 or PCV13/PCV15): • Clinical implications of the lower immunogenicity PCV20 compared with PCV13 
unknown 
• Clinical implications of improved immunogenicity of PCV15 against serotype 3* 
unknown 
*Banniettis. February 24, 2022 ACIP meeting presentation 30 
   
       
        
        
            
        
  
           
   
        
    Summary of evidence: 
Benefits, children 2–18 years with underlying conditions 
• No studies conducted among children with underlying medical conditions 
• Informed by 1 non-randomized trial (Phase III), no comparator 
• Healthy children aged 15 months to 17 years received a dose of PCV20 
• Children aged <5 years received ≥3 doses of PCV13 
• Summary of findings 
•PCV20 was immunogenic* for all 20 vaccine serotypes 1 month after 
vaccination vs. pre-vaccination. 
*Measured as IgG GMCs and GMFR and OPA GMFRs 
Pfizer unpublished data from B7471014 31 
   
      
    
   
     
    Summary of evidence: 
Harms, children 2–18 years with underlying conditions 
• Serious adverse events (SAEs) : 
• PCV20: 0.6% (n=831) 
• None were considered to be vaccine-related 
Pfizer unpublished data from B7471014 32 
           
            
     
      
  
 
 
 
  
   
         Should PCV20 without PPSV23 be recommended as an option for pneumococcal 
vaccination for U.S. children aged 2–18 years with underlying medical conditions that increase the risk of pneumococcal disease? 
Type Outcome Importance Included in evidence 
profile Certainty for children 
with underlying 
conditions 
VT-IPD Critical Yes Very Low 
Benefits VT-pneumonia Critical Yes Very Low 
VT-AOM Critical Yes Very Low 
VT-pneumococcal 
deaths Critical Yes Very Low 
Harms SAEs following 
vaccination Critical Yes Very Low 
AOM=acute otitis media, IPD=invasive pneumococcal disease, SAE=serious adverse events, VT=vaccine-type 33 
  
     
           
    
   
 
    
    
      
     Benefits and Harms 
How substantial are the desirable anticipated effects? 
 PCV20 use for children aged 2–18 years with underlying medical conditions 
□ Minimal 
 Small 
 Moderate  Large  Varies  Don’t  know □□□□□• PCV20 provides the broadest 
serotype coverage among available PCVs. 
• Unknown how substantial the protection conferred from PCV20 will be based on available data. 
• No data from this population. 
34 
  
     
            Benefits and Harms 
How substantial are the undesirable anticipated effects? 
 PCV20 use for children aged 2–18 years with underlying medical conditions 
□ Minimal 
 Small 
 Moderate  Large  Varies  Don’t  know □□□□□
35 
  
       
           
  
  
   
      Benefits and Harms 
Do the desirable effects outweigh the undesirable effects? 
 PCV20 use for children aged 2–18 years with underlying medical conditions 
□ 
□ 
□ □ □ □ Favor  s intervention* 
Favor  s current  recommendation 
Favor  s both 
Favor  s neither 
Varies Don’t  know *Intervention: PCV20 use 
Comparison: PPSV23 use after currently 
recommended PCV (PCV13 or PCV15) doses 
36 
  
       
          
  
         
     
        
       
          
       Benefits and Harms 
Do the desirable effects outweigh the undesirable effects? 
 PCV20 use for children aged 2–18 years with underlying medical conditions 
Favors Intervention (PCV20): 
• PCV20 is expected to prevent more disease compared with current recommendations (PPSV23 after recommended PCV13/15 doses) 
Favors Both (PCV20 or PPSV23 after recommended PCV13/PCV15 doses): • No data on PCV20 use in this population 
• Clinical implications of improved immunogenicity of PCV15 against serotype 3* 
unknown 
*Banniettis. February 24, 2022 ACIP meeting presentation 37 
EtR Dom  ain: Equity 
       
        
      
      
   
 
 
  
     
    Compared with coverage among children with private 
insurance only , children who were uninsured, and those 
insured by Medicaid and other insurance was lower 
≥3 PCV doses (%) ≥4 PCV doses (%) 
Private insurance only (Ref) 
(N=16,629) 96.2 90.0 
Any Medicaid (N=10,200) 91.3* 78.8* 
Other insurance (N=2,168) 91.1* 80.6* 
Uninsured (N=608) 83.9* 62.3* 
PCV=pneumococcal conjugate vaccine 
*statistically significant difference compared with Ref. 
Hill et al. MMWR 2023 39 
     
      
          
        
        
          
 
  
           
       
       
      
      
    Nationally representative PPSV23 vaccine coverage 
data among children with indications are limited 
• Vaccine coverage among children with sickle cell anemia, Michigan Medicaid program1 
• 4PCV + 1 PPSV23 at age 5 years: 64% 
• 4PCV + 2 PPSV23 at age 10 years: 53% 
• Self-administered survey of parents/guardians of children aged <18 years with 
nephrotic syndrome2 
• PPSV23 receipt: 43% 
• Data from single-center quality improvement studies among children seen in specialty 
care clinics reported 20–30% PPSV23 coverage at baseline3,4 
1. Reeves et al. Pediatric Blood & Cancer, 2018 
2. Tran et al. Frontiers in Pediatrics, 2021 
3. Mirza et al. The Ochsner Journal, 2022 40 4. Harris et al. Pediatrics, 2022 
  
  
  
  
  
 
     
 
41IPD incidence 
rate difference 
in children aged ≤17 years by census tract poverty, 
ABCs 2010–2019 
CDC ABCs, unpublished data All Serotypes PCV13 Serotypes PCV15/non-PCV13 
PCV20/non-PCV13 PCV20/non-PCV15 Nonvaccine Serotypes 
  
  
  
  
  
 
     
          
        
      
42IPD incidence 
rate difference 
in children aged ≤17 
Nonvaccine Serotypes 
years by census tract poverty, 
ABCs 2010–2019 
CDC ABCs, unpublished data PCV15/non-PCV13 
PCV20/non-PCV13 PCV20/non-PCV15 For all serotypes and PCV13 serotypes, IPD incidence rate 
difference between the highest and lowest census tract poverty categories decreased after PCV13 introduction. All Serotypes PCV13 Serotypes 
  
  
  
  
  
 
     
         
   
43IPD incidence 
rate difference 
in children aged ≤17 years by census tract poverty, 
ABCs 2010–2019 
CDC ABCs, unpublished data All Serotypes PCV13 Serotypes PCV15/non-PCV13 
PCV20/non-PCV13 PCV20/non-PCV15 Nonvaccine Serotypes Essentially no IPD incidence rate difference for the 
PCV15, non-PCV13 serotypes. 
  
  
  
  
  
 
     
         
   
       
44All Serotypes PCV13 Serotypes PCV15/non-PCV13 
IPD incidence 
rate difference 
in children aged ≤17 years by census tract poverty, 
ABCs 2010–2019 
CDC ABCs, unpublished data PCV20/non-PCV13 PCV20/non-PCV15 Nonvaccine Serotypes • IPD incidence rate difference for the additional serotypes 
contained in PCV20 remain 
• Slightly larger incidence rate difference for non-vaccine serotypes 
          
   Equity 
What would be the impact of recommending PCV20 for U.S. 
children on health equity? 
□ Reduced 
 Probably  reduced 
 Probably  n o impact 
 Probably  increased 
 Increased 
 Varie  s 
 Don’t  kno  w □
□
□
□
□
□
45 
          
      
 
           
         
  
         
 
          
  Equity 
What would be the impact of recommending PCV20 for U.S. 
children aged <2 years on health equity? 
Probably reduced: 
• New interventions are likely to be accessible to wealthy communities, first 
VFC program mitigates inequities in access to recommended vaccines 
Probably no impact: • Remaining disparities in vaccine-type disease seem to be minimal 
Probably increased: • Post-PCV13 data showed that PCV13 reduced disparities in vaccine-type disease 
VFC=Vaccines for Children 
          
        
  
  
           
  
 
         
   Equity 
What would be the impact of recommending PCV20 for U.S. 
children aged 2–18 years with underlying medical conditions 
on health equity? 
Probably no impact: 
• Risk-based recommendation is less likely to be equitable compared with routine 
vaccine recommendations. 
Probably increased: 
• PCV20 use could simplify the pneumococcal vaccine recommendations and 
improve vaccine coverage. 
        
       
  
  
  
 
    
      
      
   Summary of Work Group Interpretation of the EtR Domains (Preliminary) 
EtR Domains PCV20, <2 years (routine) PCV20, 2–18 years old 
Public Health Problem Yes 
Benefits and Harms 
a. Benefits Moderate 
b. Harms Minimal 
c. Benefit>Harm? Favors intervention/Favors both (split) 
d. Overall certainty: 
effectiveness 2 (moderate) 4 (very low) 
e. Overall certainty: safety 2 (moderate) 4 (very low) 
Equity Probably increased (different opinions) 
48 
      
          
          
          
   Acknowledgements 
• ACIP and the Pneumococcal Vaccines Work Group 
• CDC contributors and consultants: Ryan Gierke, Jennifer Farrar, Kristin Andrejko, 
Lindsay Zielinski, Emma Accorsi, Adam Cohen, Alison Albert, Noele Nelson, Pedro Moro, Elizabeth Velazquez, Marc Fischer, Katie Hamilton, Noelle Sobotka, Rebecca Morgan, Doug Campos-Outcalt 
49 
Supplementar  y Slides
GRADE  Summary  of Evidence  
Search strategy: PCV20 use in children 
No. 
Database Strategy identified 
Clinicaltrials.gov Inclusion: Relevant Phase 2, or 3 randomized controlled trials of PCV20 
• Involved human subjects 
• Reported primary data 
• Included infants and children (age ≤18 years) 
• Included data relevant to the efficacy or effectiveness or immunogenicity and safety 
outcomes being measured 
• Included data for the dosage and timing being recommended: 
o 3+1 series for infants starting the vaccine series as currently recommended 
o Catch-up vaccine schedule for older infants and children who did not start the 3+1 series 
in time 
o Use of PCV20 to complete the PCV13 series 
o Use of PCV20 in series with PPSV23 in older children with underlying conditions in series 
with PPSV23 Included  in  
GRADE 
12 3* 
Pubmed 
Medline “PCV20” or “20-valent pneumococcal conjugate vaccine” Included studies using the criteria listed above 62 1 
Additional resources Unpublished and other relevant data by consulting with the vaccine manufacturer 
2 3*      
 
          
  
  
                  
  
        
          
               
 
       
               
 
      
      
           
             
 
 
 
 
 
 
 
 
*Same trials. Unpublished data from these trials were obtained from pharmaceutical companies. 51 
         
       
    
  
      
     
  
    
   
  
      
   
   
  
  
    
   
       
   
   
 
 
 
 
  
  
  
  Included Studies: Routine PCV20 Use in Children Aged <2 years 
Author, year Study 
design Intervention Country Age Total population N Intervention N comparison Outcomes Funding source 
Phase II RCT 42–98 
Senders, 2021 in healthy full-term 
infants PCV20 @ 2, 4, 6, 
and 12 months of age US days of age at 
consent 460 232 228 Immuno-
genicity and safety Pfizer 
B7471011 Phase III RCT 
in healthy full-term 
infants PCV20 @ 2, 4, 6, 
and 12 – 15 months of age US, Puerto Rico 42–98 
days of age at 
consent 1998 1001 997 Immuno-
genicity and safety Pfizer 
US, Puerto 42–98 
B7471013 Phase III RCT in healthy infants PCV20 @ 2, 4, 6, and 12 – 15 months of age Rico, 
Canada, 
Chile, Argentin a, EU days of age at 
consent 1511 1000 551 Safety Pfizer 
52 
RCT=Randomized Controlled Trial 
Certainty assessment № of patients Results 
Certainty Importance № of 
studies Study 
design Risk of 
bias Inconsistency Indirectness Imprecision Other 
considerations Intervention comparison Relative 
(95% CI) Absolute 
(95% CI)    
      
  
 
        
   
      
  
    
   
    
    
     
   
   
     
  -Vaccine effectiveness 
21 2 RCT Not 
serious Not serious Seriousa Not serious Not serious 921-1022 910-989 • PCV20 had numerically lower 
immune responses compared with PCV13 for most of the 
13 shared serotypes. 
• PCV20 did not meet 
noninferiority criteria for some serotypes after dose 3. 
• PCV20 noninferior to PCV13 for all 13 shared serotypes after dose 4. 
• PCV20 noninferior to PCV13
b 
for all 7 additional serotypes after dose 4. Moderate Critical GRADE Summary of Findings: Routine PCV20 use in Children Aged <2 Years            
               
             
                                           
  
                    a. These are all immunogenicity studies and there are no correlates of protection for most outcomes. 
b. Compared with serotype with lowest immune response among PCV13 serotypes except for serotype 3 
References 
1. Senders S, Klein NP, Lamberth E, Thompson A, Drozd J, Trammel J, Peng Y, Giardina PC, Jansen KU, Gruber WC, Scott DA, Watson W. Safety and Immunogenicity of a 20-valent Pneumococcal Conjugate Vaccine in Healthy Infants in the United States. Pediatr Infect Dis J. 2021 Oct 
1;40(10):944-951. doi: 10.1097/INF.0000000000003277. 53 2.B7471011. A Phase 3, Randomized, double-blind trial to evaluate the safety and immunogenicity of a 20-valent pneumococcal conjugate vaccine in healthy infants 
Certainty assessment № of patients Results 
Certainty Importance № of 
studies Study 
design Risk of 
bias Inconsistency Indirectness Imprecision Other 
considerations Intervention Comparison Relative 
(95% CI) Absolute 
(95% CI) 
Serious Adverse Events (SAEs) following vaccination    
      
  
     
        
   -21 3 RCT Not Not serious Not serious Seriousa Not serious 4.5% 3.7% No vaccine-related 
serious (n=1567) (n=1376) serious adverse events Moderate Critical 
reported GRADE Summary of Findings: Routine PCV20 use in Children Aged <2 Years            
   
   
                             
               
                     
                            a. No v
accine-related serious adverse events reported 
References 
1.Senders S, Klein NP, Lamberth E, Thompson A, Drozd J, Trammel J, Peng Y, Giardina PC, Jansen KU, Gruber WC, Scott DA, Watson W. Safety and Immunogenicity of a 20-valent Pneumococcal Conjugate Vaccine in Healthy Infants in the United States. Pediatr Infect Dis J. 2021 Oct 1;40(10):944-951. doi: 10.1097/INF.0000000000003277. 2.B7471011. A Phase 3, Randomized, double-blind trial to evaluate the safety and immunogenicity of a 20-valent pneumococcal conjugate vaccine in healthy infants 3.B7471013. A Phase 3, Randomized, double-blind trial to evaluate the safety of a 20-valent pneumococcal conjugate vaccine in healthy infants. Data limited to U.S. and Puerto Rico sites. 
54 
Included Study: PCV20 Use in Children Aged 2–18 Years with Underlying 
Medical Conditions 
Author, year 
B7471014            
 
       
  
  
  
 
 
    
    
 
  
   
 
    
    
 
  
    
   
     
   
    
 Study design Intervention Country Age Total 
population N Intervention N comparison Outcomes 
Funding 
source 
Single dose PCV20 @ 15m to <24m; 15m 
previous 
vaccination ≥3 to 
<24m 209 209 N/A 
Phase III doses of PCV13 
Immuno-genicity and 
safety Pfizer Clinical Trial 
in healthy 
children, 
some previously Single dose PCV20 @ 2y to <5y; previous 
vaccination ≥3 
doses of PCV13 US 2y to <5y 216 216 N/A 
vaccinated Single dose PCV20 @ 5y to <10y 
Single dose PCV20 
@ 10 to <18y 5y to <10y 201 201 N/A 
55 10y to <18y 205 205 N/A 
GRADE Summary of Findings: PCV20 Use in Children Aged 2–18 Years 
with Underlying Medical Conditions 
Certainty assessment № of patients Results 
Certainty Importance № of 
studies Study 
design Risk of 
bias Inconsistency Indirectness Imprecision Other 
considerations Intervention comparison Relative 
(95% CI) Absolute 
(95% CI) 
Vaccine effectiveness            
   
   
      
  
 
         
   
   
    
    
     11 Non-RCT Very 
Serious 
a Not 
applicable Very 
Seriousb,c Not 
serious Not serious 752-75 7 None IgG GMCs were higher 1-
month post-PCV20 dose compared to before vaccination for 13/13 shared serotypes and 7/7 additional serotypes, for all age groups 
Very Low Critical 
                           
        
                
                a. Study design is an open label non-randomized controlled trial with no comparator group. Downgraded for lack of randomization, lack of blinding, and lack of a comparison group. 
b. Study population did not include children with underlying conditions 
c. This is an immunogenicity study and there are no correlates of protection for some critical outcomes considered 
References 
B7471014. Safety and Immunogenicity Study of 20vPnC in Healthy Children 15 Months Through 17 Years of Age 56 
GRADE Summary of Findings: PCV20 use in Children Aged 2–18 
Years With Underlying Medical Conditions 
Certainty assessment № of patients Results 
Certainty Importance № of 
studies Study design Risk of 
bias Inconsistency Indirectness Imprecision Other 
considerations PCV20 Intervention Relative 
(95% CI) Absolute 
(95% CI) 
Serious Adverse Events (SAEs) following vaccination            
    
   
       
  
     
      
   11 Non-
randomized 
trial Serious 
a Not 
applicable Seriousb Seriousc Not serious 0.6% 
(n=831) No vaccine-related 
SAEs reported Very Low Critical 
            
        
           
                a. Study design is an open label non-randomized controlled trial with no comparator group
b. Study population did not include children with underlying conditionsc. No vaccine-related serious adverse events reported; relative risk crossing 1
Reference 
B7471014. Safety and Immunogenicity Study of 20vPnC in Healthy Children 15 Months Through 17 Years of Age 
57