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CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            1 
  
De
partment of Health and Human Services  
Food and Drug Administration 
Center for Biologics Evaluation and Research  
 
CBER S
ENTINEL PROGRAM SUFFICIENCY MEMORANDUM  
 
 
From:  Joyce Obidi  
Health Scientist, CBER Surve illance Program 
Office of Biostatistics and Epidemiology (OBE)  
  
Through:  Hui-Lee Wong  
Associate Director, CBER Surveillance Program, OBE  
  
Subject:  CBER Sentinel Program Sufficiency Assessment  
  
Product:  COMIRNATY; BNT162b2 (Pfizer -BioNTech COVID -19 Vaccine)  
  
Sponsor:  Pfizer  
  
STN:  125742/0  
  
Proposed 
Indication:  Active immunization to prevent COVID -19 disease caused by SARS -
CoV -2 in individuals >16 years of age.  
  
Approval Type:  ☒  Priority        ☐ Standard review  
  
Submission Date:  May 18, 2021  
  
Action Due Date:  January 16, 2022  
 
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            2 
 1. Objectives/Scope:  
This memo reviews the capability and sufficiency of the CBER a ctive post -market risk 
identification and analysis system referred to as the CBER Sentinel Program to evaluate 
the serious risk for myocarditis and pericarditis following receipt of BNT162b2, a 
COVID- 19 Vaccine indicated for  active immunization to prevent COVID-19 disease 
caused by SARS- CoV-2 in individuals >16 years of age in lieu of a safety post- market 
requirement (PMR) study under FDAAA1. The CBER Sentinel Program covers activities 
conducted through the contract with the Harvard Pilgrim Health Care Institute, the 
current and future contracts through the Biologics Effectiveness and Safety (BEST) Initiative, and the interagency agreement with the Centers for Medicare and Medicaid 
(CMS). Please see the STN 125742/0 OBE/Divisio n of Epidemiology (D E) review of the 
Pharmacovigilance Plan (PVP ) for background on the serious risks of myo carditis and 
pericarditis , and subclinical  myoc arditis . Post -authorization safety data identified serious 
risks for myocarditis and pericarditis after COMIRNATY, with increased risk in males under 30 years of age, particularly following the second dose, and onset of symptoms 
within 7 days following vaccination. At the end of May 2021 CDC issued clinical 
considerations regarding myocarditis and pericarditis after receipt of  mRNA COVID -19 
vaccines among adolescents and young adults (
https://www.cdc.gov/vaccines/covid-
19/clinical- considerations/myocarditis.html ). The topic was presented and discussed at 
the FDA Vaccines and Related Biological Products Advisory Committee (VRBPAC) meeting on June 10, 2021 and the Advisory Committee for Immunization Practices 
(ACIP) meeting on June 23, 2021. The Emergency Use Autho rization (EUA) Fact Sheet 
was revised on June 25, 2021 to add a Warning for myocarditis and pericarditis. A 
postmarketing observational safety study(ies) is needed to assess myocarditis and 
pericarditis following administration of COMIRNATY (BNT162b2) to:  
a. Quantify the magnitude of risk by age, sex, and dose 
b. Follow up cases for recovery status and long- term sequelae  
c. Characterize subclinical cases of myocarditis  
 
2.
 CBER Sentinel Program Sufficiency Assessment:  
Determination of the sufficiency of the CBER Sentinel Program to further characterize 
the serious risk of myocarditis and pericarditis with BNT162b2  was based on the 
following factors:  
 
 
1 Under section 901 of the Food and Drug Administration Amendments Act (FDAAA), “The Secretary may not require the responsible person to 
conduct a study under this paragraph, unless the Secretary makes a determination that the reports under subsection (k)(1) and the active 
postmarket risk identification and analysis system as available under subsection (k)(3) will not be sufficient to meet the purposes set forth  in 
subparagraph (B) .”NOTE: The active post- market risk identification and analysis system under subsection (k)(3) refers to the Sentinel program.  
2 ISBT 128 is a global standard for the safe identification,  accurate labeling, and  efficient information transfer of medical 
products of human origin (including blood, cells, tissues, milk, and organ products) across disparate national and international 
health care systems. https://www.iccbba.org/isbt-128-basics  
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            3 
 2.1 Identification of exposure to BNT162b2 
 
2.2  Identification of the appropriate study population: Patients >  16 years of age 
 
2.3 Characterization of occurrence of myo carditis and pericarditis , and subclinical 
myocarditis,  with BNT162b2 
 
2.4 Identification of exposure to comparator product (when applicable) 
 
2.1  Assessment for identification of exposure to BNT162b2  
 
2.1.1. Is the CBER Sentinel Program able to identify the product (exposure) of interest?  
 
Please answer each question i – xi, including sub -questions.  Yes No 
i.  Is this the first or the only FDA -approved product for the 
indication?  ☒ ☐ 
ii.  Can the exposure be identified using a billing or reimbursement 
coding system? If yes, check all that apply: ☒ CPT  ☒ HCPCS  
☒ NDC  ☐ ICD ☐ Other: [Coding system]  ☒ ☐ 
iii.  Is the ISBT 128 coding system2 needed for the product 
identification?  ☐ ☒ 
iv.  Can the reimbursement code of the product identify the brand 
name?  ☒ ☐ 
v.  Is a history of uptake for previously approved products for the 
same indication needed? If yes, list all products:   ☐ ☒ 
vi.  Is medical chart review needed to identify or validate the 
identification of this product?  ☐ ☒ 
vii.  Are claims data sources needed for exposure identification?  ☒ ☐ 
viii.  Are electronic health record (EHR) data sources needed for 
exposure identification?  ☐ ☒ 
ix.  Are any other health record type data sources needed for 
exposure identification? If yes, all health record types needed: 
[e.g., Registries, any other health records]  ☒ ☐ 
x.  Is product lot number needed for identification of this product?  ☐ ☐ 
xi.  Is there a care setting of interest required for identification of 
this product? If yes , check all that apply:  
 
☐ Inpatient ☐ Outpatient  ☐ Emergency Room ☐ Other: 
Hospitalization  ☐ ☒ 
 
2.1.2.
 Summary for product exposure identification  
 
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            4 
 ☒ Available data sources in the CBER Sentinel Program are sufficient to identify the 
exposure of the product BNT162b2 due to reasons identified in 2.1.1.ii. Billing codes 
for BNT162b2 allows for clear ascertainment  of exposure to the product.   
 
☐ Available data sources in the CBER Sentinel Program are NOT sufficient to identify 
the exposure of the product [name]  due to reasons identified in [list all bullets from 
2.1.1.i.⸺2.1.1.xi. that support insufficiency]. 
 
2.2. Assessment for identification of the appropriate study population: Patients >  16 
years of age  
 
2.2.1.  Is the CBER Sentinel Program able to identify the study population of interest?   
 
 
2.2.2. Summary for identification of study population  
 
☒ Available data sources in the CBER Sentinel Program are sufficient to identify the 
study population of interest , patients > 16 years of age, due to reasons identified in 
2.2.1.i - 2.2.1.vi. This study population of interest has been identified in the data 
sources required of exposure (BNT162b2) and outcome (myocarditis/pericarditis ). 
 
☐ Available data sources in the CBER Sentinel Program are NOT sufficient to identify 
the study population of interest  due to reasons identified in [list all bullets from 
2.2.1.i.⸺2.2.1.vi. that support insufficiency]. 
 Please provide an answer for each question i – vi, including sub -
questions.  Yes No 
i.  Does age need to be identified? If yes, list the inclusion and 
exclusion criteri a.. Check all that apply for the level of 
granularity in ☐ Days  ☐ Months  ☒ Years  ☒ ☐ 
ii.  Does sex need to be identified? If yes, list the inclusion [List 
the sex to be included] and exclusion criteria  [List the sex to 
be excluded].  ☐ ☒ 
iii.  Does race need to be identified? If yes, list the inclusion [List 
race to be included] and exclusion criteria [List race to be 
excluded]  ☐ ☒ 
iv.  Can the study population be identified in the data sources 
required for the exposure and outcome identification? ☒ ☐ 
v.  Was this population previously identified within the CBER 
Sentinel Program activities?  ☒ ☐ 
vi.  Is there a requirement for linking mothers to their newborns in 
the data sources?  ☐ ☒ 
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            5 
 2.3 Assessment for characterization of occurrence of myocarditis and pericarditis, and 
subclinical myocarditis  
 2.3.1 Is the CBER Sentinel Program able to identify the outcome(s) of interest?  
 
Please provide an answer for each question i – xi, including sub -
questions.  Yes No 
i.  Can the outcome of interest be identified using a billing or 
reimbursement coding system? If yes, check all that apply: ☒ ICD  
☐ CPT  ☐ Other: Medical Record Review   ☒ ☐ 
ii.  Are there surrogate data elements or biomarkers that can assist to 
identify the outcome of interest? If yes , check all that apply: 
☐ Laboratory Test Results  ☐ Prescription drug ☐  Order of lab 
test ☐  Order of other diagnostic modalities ☐ Other: [Data 
element/Biomarker]  ☐ ☒ 
iii.  Are there specific care settings in which this outcome is 
identified? If yes, check all that apply:  ☒ Inpatient ☒ Outpatient  
☒ Emergency Room  ☒ Other: Hospitalization  ☒ ☐ 
iv.  Was this outcome previously identified within the CBER Sentinel 
Program activities? If yes , in what population was it used? It was 
used in a similar population of Medicare beneficiaries 65y and 
older.   ☒ ☐ 
v.  Is there a validated and acceptable algorithm available in the 
literature to identify the outcome of interest? If yes , list the PPV  
[PPV] and describe the population in which it was validated : ☐ ☒ 
vi.  Is a minimum follow -up time needed to identify the outcome of 
interest? If yes, what is the required follow-up period? 3-6 months  ☒ ☐ 
vii.  Is medical chart review required to identify or validate the 
identification of the outcome?  ☒ ☐ 
viii.  Is the prevalence of the outcome known? If yes, list background 
rates . 0.95-2/16 per 100,000 PY  in Gubernot 2021  ☒ ☐ 
ix.  Are claims data sources needed for outcome characterization?  ☒ ☐ 
x.  Are electronic health record (EHR) data sources needed for 
outcome characterization?  ☒ ☐ 
xi.  Are any other health record type data sources needed for outcome 
characterization? If yes, all health record types needed:  Registries  ☒ ☐ 
 2.3.2 Summary of outcome characterization  
 
              
     
        
    
 
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            6 
 ☒ Available data sources in the CBER Sentinel  Program are NOT sufficient to identify the 
outcomes of myocarditis and pericarditis  due to reasons identified in 2.3.1.vi. ⸺2.3.1.vii i. 
Based on the prevalence of background rates estimated in the CBER Sentinel data sources and 
the number of observed myocarditis/pericarditis events in the CBER Sentinel Program on -
going  near -real time surveillance, the CBER Sentinel data sources are currently not 
sufficiently powered to assess the magnitude of risk for the 12 -30 years old that has been 
reported in VAERS in an epidemiology study (e.g., self- controlled analyses).  CBER Sentinel 
will continue to monitor these safety outcome s. In order to follow up  cases for recovery status 
and long- term sequelae, a minimum follow up time of 3 -6 months is required. CBER Sentinel 
data sources do not have sufficient longitudinal data on patients to conduct this type of 
analysis. Additionally, a study of subclinical myo carditis using CBER Sentinel data sources is 
not feasible because of the absence of a definition of subclinical myocarditis and unknown background incidence of troponin abnormalities . 
  
2.4. Assessment for identification of exposure to comparator product (when applicable) : 
NOT APPLICABLE  
 
2.4.1.
 Is the CBER Sentinel Program able to identify the required comparator product?  
Respond to the questions below, if applicable.  
 
Please provide an answer for each question i – xi, including sub -
questions  Yes No 
i.  Is a comparator product needed for the assessment? If no, 
skip to section III for Recommendation . If yes, list all 
products:  ☐ ☐ 
ii.  Can the comparator product be identified using a billing 
reimbursement code? If yes, check all that apply: ☐ CPT  
☐ HCPCS  ☐ NDC  ☐ ICD ☐ Other:[Billing 
reimbursement code]  ☐ ☐ 
iii.  Can the comparator product be exclusively identified using 
the billing reimbursement codes?  ☐ ☐ 
iv.  Is the ISBT 128 coding system2 needed for the comparator 
product identification?  ☐ ☐ 
v.  Can the reimbursement code of the comparator product 
identify the brand name?  ☐ ☐ 
vi.  Is medical chart review needed to identify or validate the 
identification of this comparator product?  ☐ ☐ 
vii.  Are claims data sources needed for exposure identification 
of the comparator product?  ☐ ☐ 
viii.  Are electronic health record (EHR) data sources needed for 
exposure identification of the comparator product?  ☐ ☐ 
CBER Sentinel Program Sufficiency Memo: BNT162b2 (COVID- 19 Vaccine) /STN 125742 
 
Last Updated on January 29 , 2019                                                                                                                            7 
 Please provide an answer for each question i – xi, including sub -
questions  Yes No 
ix.  Are any other health record type data sources needed for 
exposure identification of the comparator product? If yes , 
list all health record types needed: [e.g., Registries, any 
other health records]  ☐ ☐ 
x.  Is product lot number needed for identification of this 
comparator product?  ☐ ☐ 
xi.  Is there a care setting of interest for identification of this 
comparator product? If yes , check all that apply: ☐ 
Inpatient ☐ Outpatient  ☐ Emergency Room ☐ Other: 
Hospitalization  ☐ ☐ 
 
2.4.2.
 Summary for comparator exposure identification  
 
☐
 Available data sources in the CBER Sentinel Program are sufficient to identify the 
comparator product due to reasons identified in [list all bullets from 2.4.1.i. ⸺2.4.1.xi. 
that support sufficiency].  
 
 ☐ Available data sources in the CBER Sentinel Program are NOT sufficient to identify 
the comparator product due to reasons identified in [list all bullets from 
2.4.1.i.⸺2.4.1.xi. that support insufficiency]. 
 
3. Recommendation:  
 
☐ The CBER Sentinel Program is sufficient  to assess the serious risk of [describe] 
associated with [product] at this time. [Summarize all bullets 2.1. ⸺2.4. that support 
sufficiency]  
 
☒ The CBER Sentinel Program is NOT sufficient to assess the serious risk s of 
myocarditis and pericarditis , and subclinical myocarditis  associated  with 
COMIRNATY ( BNT162b2) in lieu of  PMR safety stud ies under FDAAA.  At the time 
of BLA approval, the data sources in the CBER Sentinel Program are not sufficient to 
identify the outcome s due to lack of sufficient power to assess the magnitude of risk in 
patients 12 -30 years of age. In addition, CBER Sentinel Program is not sufficient to 
follow up cases for recovery status and long- term sequelae, or for identification and 
characterization of subclinical myocarditis cases.